Huntington's disease-causing DNA repeat mutations reversed in the lab

An international team of researchers identifies a compound that corrects genetic abnormalities involved in the onset and progression of Huntington's disease for which there is no definitive treatment. They successfully reversed disease-causing DNA expansion mutations with no off-target effects in the lab. They hope that their discovery may help treat other DNA repeat diseases like myotonic dystrophy.

from Latest Science News -- ScienceDaily https://ift.tt/385ZPtZ

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